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Articles published by Cure Rare Disease
Cure Rare Disease Awarded $7.4 Million CIRM Grant to Advance Gene Therapy for Limb-Girdle Muscular Dystrophy Type 2i/R9
December 15, 2025
From
Cure Rare Disease
Via
Business Wire
Cure Rare Disease Secures FDA Orphan Drug Designation for Investigational Gene Therapy to Treat Limb-Girdle Muscular Dystrophy Type R9 (LGMD2i/R9)
September 24, 2025
From
Cure Rare Disease
Via
Business Wire
Cure Rare Disease Receives FDA Feedback on Limb-Girdle 2i/R9 Gene Therapy Program Following Successful Pre-IND Meeting
June 24, 2025
From
Cure Rare Disease
Via
Business Wire
Cure Rare Disease Welcomes New Scientific and Strategic Leaders to Advance Therapies for Ultra-Rare Conditions
June 09, 2025
From
Cure Rare Disease
Via
Business Wire
Cure Rare Disease Receives Orphan Drug Designation from FDA for Investigational Therapy Targeting Spinocerebellar Ataxia Type 3 (SCA3)
May 14, 2025
From
Cure Rare Disease
Via
Business Wire
We Row For William: 157 Miles, One Nonstop Journey of Hope
April 03, 2025
From
Cure Rare Disease
Via
Business Wire
Cure Rare Disease Awarded $5.69 Million CIRM Grant to Advance Gene Therapy for Spinocerebellar Ataxia Type 3
February 06, 2025
From
Cure Rare Disease
Via
Business Wire
Cure Rare Disease Appoints Brittany Stineman as Chief Advancement Officer
December 18, 2024
From
Cure Rare Disease
Via
Business Wire
Cure Rare Disease Expands Leadership Team and Board of Directors to Advance Mission
June 17, 2024
From
Cure Rare Disease
Via
Business Wire
Cure Rare Disease Welcomes Leading Experts to Scientific Advisory Board
March 20, 2023
From
Cure Rare Disease
Via
Business Wire
Cure Rare Disease Receives Muscular Dystrophy Association Grant
February 16, 2023
From
Cure Rare Disease
Via
Business Wire
Cure Rare Disease Acquires Laboratory Space for New Headquarters in Connecticut
September 29, 2022
From
Cure Rare Disease
Via
Business Wire
Cure Rare Disease Receives FDA Approval to Administer First-in-Human CRISPR Therapeutic
August 10, 2022
From
Cure Rare Disease
Via
Business Wire
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